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  • Duchenne Muscular Dystrophy

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#1
Cooperative International Neuromuscular Research G
Cooperative International Neuromuscular Research G
Center for Genetic Medicine Research, Children’s National Medical Center, Washington, DC 20010, USA Department of Neuroscience, University of Padova, 35128 Padova, Italy The ...
Known for star star star star star
Muscular Dystrophy | Coenzyme Q10 | Muscle Strength | Boys Dmd
#2
NS Pharma, Inc.
NS Pharma, Inc.
Known for star star star star star_half
Duchenne Muscular | Ambulant Boys | Dystrophy Dmd | Ns-065 Ncnp-01

#3
Newcastle University
Newcastle University
Known for star star star star star_half
Physical Activity | Colorectal Cancer | Young People | Sleep Apnoea
#4
Nippon Shinyaku Co., Ltd.
Nippon Shinyaku Co., Ltd.
Known for star star star star star_half
Duchenne Muscular | Ambulant Boys | Ns-065 Ncnp-01 | Assess Safety
#5
Kate Bushby
Kate Bushby
Department of Human Genetics, University of Newcastle upon Tyne, 19 Claremont Place, NE24AA, Newcaste upon Tyne, UK
Known for star star star star star_half
Muscular Dystrophy | Examination Performed | Corticosteroids Dmd | Dystrophin Gene
#6
Summit Therapeutics
Summit Therapeutics
Known for star star star star star_half
Smt C1100 | Difficile Infection | Duchenne Muscular | Paediatric Male
#7
Kevin Flanigan
Kevin Flanigan
Known for star star star star star_half
Duchenne Muscular | Gene Transfer | Exon Eteplirsen | Dystrophy Trial
#8
Santhera Pharmaceuticals
Santhera Pharmaceuticals
Known for star star star star star_half
Muscular Dystrophy | Phase Iii | Hereditary Optic | Term Safety
#9
Genethon
Genethon
Known for star star star star star_half
Gene Therapy | Muscular Dystrophy | Chronic Granulomatous | Lentiviral Vector
#10
Günther Bernert
Günther Bernert
Department of Pediatrics, Neuropediatrics, Kaiser Franz Josef Krankenhaus mit Gottfried von Preyer Children Hospital, Vienna, Austria.
Known for star star star star star_half
Systemic Corticosteroids | Muscular Dystrophy | Ambulatory Duchenne | Phase Iii
#11
Chaitanya Hospital And Nursing Home
Chaitanya Hospital And Nursing Home
Known for star star star star star_half
Bone Marrow | Derived Autologous | Muscular Dystrophy | Mono Nuclear
#12
Anant E Bagul
Anant E Bagul
Known for star star star star star_half
Bone Marrow | Derived Autologous | Muscular Dystrophy | Mono Nuclear
#13
Institute for Neuromuscular Research
Institute for Neuromuscular Research
Known for star star star star star_border
Muscle Strength | Duchenne Muscular | Phase Iii | Botulinum Toxin
#14
Han Phan
Han Phan
Known for star star star star star_border
Systemic Corticosteroids | Duchenne Muscular | Zyn002 Administered | Pamrevlumab Combination
#15
Maria Grazia D'Angelo
Maria Grazia D'Angelo
From Sorbonne Université (G.C., C.E., B.F., M.-L.M., F.M., M.P., C.-S.D., G.S., A.D.), Institut du Cerveau et de la Moelle épinière (ICM), AP-HP, INSERM, CNRS, University ...
Known for star star star star star_border
Systemic Corticosteroids | Muscular Dystrophy | Ambulatory Duchenne | Pamrevlumab Combination
#16
Diana M Escolar
Diana M Escolar
Known for star star star star star_border
Muscular Dystrophy | Creatine Monohydrate | Ht-100 Long | Term Safety
#17
Stem Cells Arabia
Stem Cells Arabia
Known for star star star star star_border
Stem Cells | Bone Marrow | Purified Autologous | Muscular Dystrophy

 

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A Phase 3, Randomized, Double-Blind, Trial Of Pamrevlumab (Fg-3019) Or Placebo In...

[ CLINICAL_TRIAL ] ... non-ambulatory Duchenne muscular dystrophy (age 12 years and older). Detailed Description This is a global, randomized, double-blind trial of pamrevlumab or placebo in combination with ...
Known for star star star star star
Systemic Corticosteroids | Ambulatory Duchenne | Muscular Dystrophy | Pamrevlumab Combination

A Phase 3, Randomized, Double-Blind, Trial Of Pamrevlumab (Fg-3019) Or Placebo In...

[ CLINICAL_TRIAL ] ... with Duchenne muscular dystrophy (age 6 to <12 years). Detailed Description This is a global, randomized, double-blind, trial of pamrevlumab or placebo in combination with systemic ...
Known for star star star star star
Systemic Corticosteroids | Muscular Dystrophy | Pamrevlumab Combination | Ambulatory Duchenne

A Double-Blind, Placebo-Controlled, Multi-Center Study With An Open-Label...

[ CLINICAL_TRIAL ] The main objective of this study is to evaluate the efficacy of SRP-4045 and SRP-4053 compared to placebo in participants with DMD with out-of-frame deletion mutations amenable to skipping exon ...
Known for star star star star star_half
Duchenne Muscular | Srp-4045 Srp-4053 | Dmd Frame | Skipping Exon

Carvedilol For The Prevention Of Minor Cardiac Damage And Cardiac Function In...

[ CLINICAL_TRIAL ] ... with Duchenne muscular dystrophy is associated with minor cardiac damage as indicated by elevation of plasma cardiac troponin I (cTnI). The purpose of this study is to investigate whether ...
Known for star star star star star_half
Cardiac Damage | Muscular Dystrophy | Dysfunction Minor | Ctni Plasma

Performance Of Upper Limb (Pul) In Duchenne Muscular Dystrophy. Upper Limb...

[ CLINICAL_TRIAL ] ... in Duchenne muscular dystrophy (DMD) is quite scanty. While there have been considerable advances for ambulant DMD boys, no prospective study has so far been devoted to outcome measures in ...
Known for star star star star star_border
Upper Limb | Muscular Dystrophy | Measures Function | Ambulant Dmd

A Phase Iii Double-Blind, Randomised, Placebo-Controlled Study Of The Efficacy,...

[ CLINICAL_TRIAL ] The aim of this Phase III study was to assess the efficacy of idebenone on pulmonary function, motor function, muscle strength and quality of life in patients with DMD. Furthermore, the safety ...
Known for star star star star star_border
Phase Iii | Duchenne Muscular | Muscle Strength | Dmd Safety

Biomarker For Duchenne Muscular Dystrophy: An International, Multicenter,...

[ CLINICAL_TRIAL ] ... for Duchenne Muscular Dystropy (DMD) and to explore the clinical robustness, specificity, and long-term variability of these biomarker/s. Detailed Description Duchenne Muscular Dystrophy ...
Known for star star star star star_border
Duchenne Muscular | Dystrophin Dmd | Observational Longitudinal | International Multicenter

Determining Biomechanical And Morphological Factors That Affect Children With...

[ CLINICAL_TRIAL ] ... (Duchenne muscular Dystrophy) is a pejorative event. Biomechanical and morphological unknowledge about the loss of the walk ability in children with DMD is an obstacle in reeducative, ...
Known for star star star star star_border
Muscular Dystrophy | Walk Ability | Children Dmd | Biomechanical Morphological

A Randomized, Double-Blind, Placebo-Controlled, Multiple Dose Study With An...

[ CLINICAL_TRIAL ] ... therape
Known for star star star star star_border
Oral Ifetroban | Muscular Dystrophy | Respiratory Cardiomyopathy | Open Extension

Endomysial Fibrosis, Muscular Inflammatory Response And Calcium Homeostasis...

[ CLINICAL_TRIAL ] ... muscl
Known for star star star star star_border
Muscular Dystrophy | Endomysial Fibrosis | Calcium Homeostasis | Targeted Pharmacotherapy